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Addiction | Alcohol | Drugs
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Adolescents
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Athletics | Exercise
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Pregnancy
The process by which a female produces an offspring in their womb once the male and female zygotes have combined into a single embryo until birth.
Embryo
The offspring in the womb, from the moment 2 zygotes co-exist up until the 11th week of pregnancy, is medically referred to as "Embryo"
Fetus
The offspring in the womb, beginning on the 11th week of pregnancy, has graduated from "Embryo" to "Fetus"
Newborn
The offspring, now emerged from the womb and ending the female's pregnancy.
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Cancer
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Children
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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COVID-19
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Disease
An abnormality caused due to pathophysiological response to external or internal factors.
Disorder
A disruption in normal functioning of mind or body due to a disease, genetic factor or trauma.
Syndrome
A set or collection of various identifying signs and symptoms that characterizes a certain disease or disorder.
Condition
An abnormal state of physical or mental health that interferes with usual activities or the feeling of well-being.
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
[Please complete our feedback form]
Food | Obesity
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
[Please complete our feedback form]
Girls ♀ Women
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Infections | Immune System
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Injury | Pain | Violence
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Medication | Treatment | Therapy | Surgery
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Mental Health | Wellbeing | Stress | Sleep
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Myths | Fake News | Science Mistrust
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Physical Health | Human Body | Sex
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Products | Supplements
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Racism | Inequality
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Science
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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Technology
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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YouTube #Shorts
Discovering Zolgensma for SMA: What goes into making the most expensive drug on the market?
3.7 Million Dollars CAN for a drug? It’s the most expensive medication on the market!! Zolgensma is a single dose medication to relieve the symptoms of Spinal Muscular Atrophy (SMA) in newborns and young children. But how can a drug cost this much? How do scientists even make it? Watch this video to learn about the drug discovery process through the discovery and making of Zolgensma. The drug discovery and manufacturing process is incredibly detailed and extensive.
First, they must Research the specific illness and what known compounds are able to relieve symptoms and potentially lead to a cure. With SMA there is a missing SMN1 gene that leads the child to experience muscle weakness and deterioration. With the knowledge and research gained, the next stage of the drug discovery process is Pre-clinical trials. AAV Therapy was developed as a treatment for SMA and other muscular and nervous system diseases. Specifically, the AAV9 vector can deliver the missing gene to motor neurons in the human body. The success of this medication was tested countless times via the third stage of drug discovery, Clinical Trials. The creators of Zolgensma also held their own clinical trials in children, that they had called START and STR1VE. After all the research and data is collected, the final step is FDA Approval. Zolgensma is currently approved in the United States, Japan and all 27 European nations. Health Canada has yet to approve this drug.
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